Search for Clinical Trial Results
Lysosomal Storage Diseases - 50 Studies Found
Status | Study |
Terminated |
Study Name: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases Condition:
Date: 2008-04-03 Interventions: Biological: ALD-101 A subpopulation of cord blood cells composed of cells that express a high level of t |
Recruiting |
Study Name: Biomarker for Patient With Cystinosis Disease or Highly Suspected for Cystinosis Disease Condition:
|
Terminated |
Study Name: Extension Study of Intrathecal Enzyme Replacement Therapy for MPS I Condition:
|
Completed |
Study Name: A Study of Intrathecal Enzyme Therapy for Cognitive Decline in MPS I Condition:
|
Recruiting |
Study Name: Biomarker for Metachromatic Leukodystrophy Disease Condition:
Date: 2012-02-21 |
Recruiting |
Study Name: Biomarker for Metachromatic Leukodystrophy Disease Condition:
Date: 2012-02-21 |
Recruiting |
Study Name: Biomarker for Pompe Disease Condition:
Date: 2011-10-21 |
Completed |
Study Name: Cardiopulmonary Exercise Test to Quantify Enzyme Replacement Response in Pediatric Pompe Disease Condition: Enzyme Replacement Therapy in Pompe Disease Date: 2017-04-30 |
Not yet recruiting |
Study Name: Search for Serum/Plasma Biomarkers in Pompe's Disease Condition:
Date: 2017-01-27 Interventions: Drug: Enzyme Replacement Agent Patients will be treated following the decision of their doctors. The inv |
Not yet recruiting |
Study Name: A Study to Assess Safety and Efficacy of NeoGAA Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa Condition: Glycogen Storage Disease Type II-Pompe's Disease Date: 2016-12-20 Interventions:
|